What is the most expensive medicine in the world? The United States Food and Drug Administration (FDA) approved a therapy to treat hemophilia B in adults. It will cost 3.5 million dollars per dose.
Hemgenix is a gene therapy for adults with hemophilia B, a rare disease, which makes people vulnerable to bleeding in joints, muscles and internal organs, since they do not produce the protein needed to develop blood clots.
So far, treatments for this condition include lifelong prophylactic infusions of factor IX, which replace or supplement low blood clotting levels.
In his case, Hemgenix, developed by CSL Behring, is designed to be a single dose.
How does the most expensive medicine in the world work?
According to the pharmaceutical company’s statement, hemophilia B is a rare bleeding disorder caused by a defect in a single gene, which results in insufficient production of factor IX, the protein that helps blood clots form.
Treatments for moderate to severe hemophilia B include prophylactic infusions of factor IX replacement therapy to temporarily replace or supplement low blood clotting factor levels, and while these therapies are effective, people with hemophilia B must adhere to strict lifelong infusion schedules.
CSL Behring
The new therapy will cause people living with this genetic disorder to produce their own factor IX, which may reduce the risk of bleeding.
The company responsible for the treatment reported that the price of Hemgenix will be 3.5 million dollars after receiving approval from the authorities.
In this sense, the Institute for Clinical and Economic Review, an organization that analyzes the value of medicines and other medical products, confirmed to CNN that it is the most expensive therapy in the world.
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